Lentiviral Hematopoietic Stem Cell Gene Therapy Benefits Metachromatic Leukodystrophy

By A. Biffi, E. Montini, L. Lorioli, M. Cesani, F. Fumagalli, T. Plati, C. Baldoli, S. Martino, A. Calabria, Sabrina Canale and 27 more. Science, 2013

1,156 citations recorded by the source corpus.

Subfields: Genetics, Molecular Biology

View Paper: https://www.semanticscholar.org/paper/7e870bdf8ccfa6043e460b26f6fcf61282fbbb18

Citations in the corpus

• Gene therapy comes of age (2018, neutral): “leukodystrophy LV ARSA (117, 154) San Raffaele Telethon Institute of”