Gene therapy for immunodeficiency due to adenosine deaminase deficiency.
By A. Aiuti, F. Cattaneo, S. Galimberti, U. Benninghoff, B. Cassani, Luciano Callegaro, S. Scaramuzza, G. Andolfi, Massimiliano Mirolo, I. Brigida and 20 more. New England Journal of Medicine, 2009
949 citations recorded by the source corpus.
Subfields: Genetics, Molecular Biology, Physiology
View Paper: https://www.semanticscholar.org/paper/06c5ea06bdb1369f7e7e6003d557ce7fa82a3db4
How researchers see this paper
The researchers whose trusted networks rank it highest, strongest advocate first. Every researcher gets a different order.
In Molecular Biology
Citations in the corpus
- Gene therapy clinical trials worldwide to 2012 – an update (2013, background): “A similar trial, targeting metachromatic leukodystrophy, is also treating patients in Milan [26].”
- Zinc finger nuclease-mediated CCR5 knockout hematopoietic stem cell transplantation controls HIV-1 in vivo (2010, positive): “In addition, the experience of autologous HSC transplantation in gene therapy for patients with genetic diseases such as ADA-SCID (59–60), chronic granulomatous disease (61) and X-linked adrenoleukodystrophy (62), is that non-myeloablative conditioning can be used to facilitate engraftment of…”